rare genetic disease

8-Year-Old Walks Again After Drug Trial for HPDL Deficiency

8-Year-Old Walks Again After Drug Trial for HPDL Deficiency

15 Jul 2025

4 min read

Race Against Time: Parents Struggle to Fund Rs 16 Crore Treatment for Baby’s Rare Disorder

Race Against Time: Parents Struggle to Fund Rs 16 Crore Treatment for Baby’s Rare Disorder

Priyanka Pandey

08 Jul 2024

2 min read

US FDA Approves First Gene Therapy to Treat Children with Rare Genetic Disease

US FDA Approves First Gene Therapy to Treat Children with Rare Genetic Disease

Lavanya Beeraboina

22 Mar 2024

3 min read

18-month-old's Liver Saves 14-year-old

18-month-old's Liver Saves 14-year-old

08 Jan 2024

2 min read

A Rare Genetic Condition with an Even Rarer Treatment

A Rare Genetic Condition with an Even Rarer Treatment

27 Aug 2023

5 min read

Scientists Create First Humanised Mouse Model for Rare Genetic Disease

Scientists Create First Humanised Mouse Model for Rare Genetic Disease

16 May 2023

2 min read

CRISPR Technology Improves Huntington’s Disease

CRISPR Technology Improves Huntington’s Disease

13 Dec 2022

3 min read

Study: Rare Genetic Condition to Tackle Colorectal Cancer

Study: Rare Genetic Condition to Tackle Colorectal Cancer

18 Aug 2022

2 min read

Telangana baby with rare genetic disease given Rs 16 crore drug

Telangana baby with rare genetic disease given Rs 16 crore drug

10 Aug 2022

2 min read

Medbound Times

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